RSS Worldwide Bio News

  • Phase 3 Trial Testing Pamiparib as Maintenance Therapy for Ovarian Cancer Recruiting Patients in China
    This post was originally published on this site BeiGene has started enrollment in its Phase 3 clinical trial evaluating the investigational PARP inhibitor pamiparib (BGB-290) as a maintenance therapy for ovarian cancer patients who are responding to platinum-based chemotherapy. The trial (NCT03519230) is expected to include 216 adult women with confirmed high-grade serous or endometrioid ovarian cancer, […]
  • Aplidin-Dexamethasone Combo Improves Survival in Advanced Multiple Myeloma Patients, Phase 3 Trial Reports
    This post was originally published on this site Combining Aplidin (plitidepsin) with dexamethasone significantly extends their survival in heavily pretreated multiple myeloma patients compared to dexamethasone alone, data from a Phase 3 trial show. PharmaMar, Aplidin’s maker, presented these findings in an oral presentation at the recent 2018 American Society of Clinical Oncology (ASCO) Annual Meeting  in […]
  • Imbruvica-Rituxan Combo Significantly Delays Progression of Rare Type of Lymphoma in Phase 3 Trial
    This post was originally published on this site A combination of Imbruvica (ibrutinib) and Rituxan (rituximab) significantly extends the time to disease worsening or death in patients with a rare type of lymphoma called Waldenström’s macroglobulinemia, a Phase 3 trial shows. While the approach failed to improve survival, the findings prompted Janssen — Imbruvica’s maker — to […]
  • New Blood Test Could Predict Cerebral Palsy Risk in Premature Babies, Study Suggests
    This post was originally published on this site A blood test that identifies changes in specific molecules through a tiny amount of blood collected days to weeks after birth could be used to predict the risk of cerebral palsy in premature babies, a study suggests. The study, “MicroRNA Profile Differences in Neonates at Risk for […]
  • #ECFS2018 – Potential CFTR Corrector PTI-801, Plus Orkambi, Seen to Treat CF Patients in Phase 1 Trial
    This post was originally published on this site Treatment for 14 days with Proteostasis Therapeutics’ PTI-801 in cystic fibrosis (CF) patients also being treated with Orkambi (lumacaftor/ivacaftor) led to statistically significant improvements in sweat chloride, body mass index, and rescued blood glucose levels in a subgroup of patients with diabetes, Phase 1 trial data show. PTI-801 is being […]
  • New Immunotherapy Rid Patient of Cancer in Breast, Everywhere Else, Study Reports
    This post was originally published on this site A new immunotherapy method that targets a patient’s tumor cell mutations led to a complete and lasting regression of breast cancer in a woman who had failed all other treatments, a study reported. The woman, whose disease already had spread to other organs, was free from cancer more […]
  • #ECFS2018 – Kalydeco’s Benefits Include Lower Risk of Death and Pulmonary Flares, Real-world Data Shows
    This post was originally published on this site Real-world results from the largest analyses of Vertex Pharmaceutical’s cystic fibrosis’ treatment Kalydeco (ivacaftor) done in CF patients to date confirm the therapy’s ability to significantly lower the risks of mortality, transplants, hospitalization, and pulmonary exacerbations compared to untreated patients. These results were presented today at the 41st European Cystic Fibrosis […]
  • Reclaim Your Spoons: Tips for Staying Organized with Cerebral Palsy
    This post was originally published on this site Hey everyone, a couple things before I get into this column: First, this month I plan to roll out audio with my column so I can extend my “readability” and be more accessible to all of you. Next, I want to talk a little bit about what […]
  • SMA and Accessibility at the Happiest Place on Earth
    This post was originally published on this site My father once made a promise to me as a little girl. I had been in the hospital’s intensive care unit for yet another respiratory infection, and he wanted to give me an incentive to get better. I’ve always operated best when having a goal to attain, […]
  • My MS Medical Bills: Trust, but Verify the Charges
    This post was originally published on this site “Trust, but verify” was a key concept during the U.S.-Soviet nuclear negotiations of the 1980s. “Trust,” President Ronald Reagan would say, “but verify” that what’s being said is actually being done. I apply that same concept to my bank, trusting that it has all of my checking […]